- IMMUNE RESPONSE TO BRAIN MYELIN in Autistic Children -


Autism is generally believed to be a behavioral syndrome that includes abnormalities of language and thinking skills; repetitive behavior such as rocking; abnormal responses to sensations, people, events and objects; and self- injurious behavior. What causes the syndrome is not known. A few years ago, we hypothesized that one possible cause of autism may involve faulty immune regulation, in particular, autoimmunity ( 1,2 ).
To further understand the role of immune factors, we have recently studied immune response ( or antibodies ) to myelin basic protein ( MBP ), which is a protein component of the brain myelin. The myelin is a covering sheath that is necessary for the normal flow of nerve impulses from one nerve cell to another, and defects in this function would dramatically alter brain activity and behavior.
In this study, the testing of 33 autistic children ( less than 11 years of age ) was compared with that of 18 age-matched normal children. The diagnosis of autism was made by at least one pediatric psychiatrist and one clinical child psychologist using the DSM-III-R guidelines of the American Psychiatric Association, Washington, D.C. Since nearly 60% of autistic children show mental retardation ( MR IQ of 70 or lower ), 20 children with MR due to unknown causes and 12 children with Down syndrome ( DS ) were also studied as the disease controls.
From each donor a 5 ml blood sample was drawn and the serum separated from the blood cells. The testing for serum antibodies to MBP was performed with the technique of protein-immunoblotting. When the serum contained antibodies to MBP, a positive reaction was seen by a protein band.
Screening for these antibodies showed that they were found in 19 of 33 ( 58% ) sera from autistic children as compared to only 7 of 50 ( 7% ) sera from the control children.
This result indicated that the autistic children have about 8.3 times greater incidence of antibodies to MBP than the control children. Since none of the 12 DS children and only 3 of 20 MR children showed this antibody- positive reaction, it may be concluded that the mental retardation in autistic children is not related to the production of antibodies to MBP.
Immunological testing of autistic children has shown certain FEATURES that are also found in patients with autoimmune diseases such as systemic lupus erythematosus ( SLE ), thyroid disease ( TD ), ankylosing spondylitis ( AS ), rheumatoid arthritis ( RA ), insulin-dependent diabetes ( IDD ), and multiple sclerosis ( MS ).
These are:
( a ) genetic predisposition-autism shows a greater concordance rate in monozygotic twins than in the normal population;
( b ) gender factor-autism is 4 or 5 times more common in boys than in girls;
( c ) triggering by microorganisms-rubella virus and cytomegalovirus infections have been indirectly linked to autism;
( d ) maternal factors-maternal antibodies in autism were detected by us ( 3 );
( e ) major histocompatibility ( MHC ) association- autism displays genetic linkage with immunogenetic factors located on chromosome 6, as recently discovered by our group ( 4 ); and
( f ) immune activation-this was recently observed by us in autism ( 5 ).
Taken collectively, the aforementioned parallels between autism and other autoimmune diseases suggest that autoimmunity may be a critical factor in the cause of autism. An essential part of the autoimmune mechanism should involve antibody-mediated immune response or antibodies against brain, the affected organ in autism. In this respect, a few recent studies in autism have found evidence of antibodies to brain tissue antigens, e.g., MBP ( this report ), neurofilament proteins ( 2 ),
and serotonin receptor ( 6 unpublished data ).
Antibodies to MBP may have some pathological relevance since abnormal cell-mediated immune response ( involving a soluble factor but not antibodies ) to this protein was previously detected by another group of researchers ( 7 ),
suggesting that autistic children somehow develop inappropriate immune responses to this brain protein. Brain-reactive antibodies and the increased serum levels of IgG3 antibody ( 8 ),
which selectively activates complement function via classical pathway ( another type of immunity ), could be an important first step in the activation of complement-mediated nerve cell damage, thereby altering their ability to perform normal function of nerve impulse transmission. Despite numerous behavioral problems, research into the brains of autistic children has been hampered by the lack of available brain biopsies or autopsies. Based on a very limited number of case studies, anatomical abnormalities in certain parts of the brain have been found, but the findings are not suffiently consistent to permit any firm conclusion. While the pathological data are scarce, we know virtually nothing about the neurochemistry ( neurotransmitter function ) of the autistic brain. Whatever the pathological abnormalities might be, it is generally believed that the anatomical defects are the results of abnormal development rather than damage following full development of the brain in autistic children ( 9 ).
At present, the relationship between antibodies to MBP and autism is not understood. However, we hypothesize that the development of this immune response may be the basis of autoimmune pathogenesis in some cases of autism. At birth, there is very little myelin in the brain, and the synthesis of myelin may not be complete until the age of 10 years or older in the normal child ( 10 ). Moreover,
It has been suggested that some children with learning disabilities ( LD ) may have delayed or incomplete myelin development ( 11 ).
In light of the above, it is conceivable that if an immunological assault were to occur before birth or during infancy or childhood, it could lead to poor myelin development or abnormal function of the nerve fiber myelin. This line of thinking, as we postulate in this report, may be an important step in the future understanding of the pathological basis of Autism.

by Vijendra K. Singh, Reed P. Warren, Dennis Odell: Utah State Univ, 1992 | Autism Info